February, 2003
© 2000, 2001, 2003 Scott S. Emerson, M.D., Ph.D.
Phases of Clinical Trials: 3
Phase I Clinical Trials
Phase I: Initial safety / dose finding in humans
Goals:
·Pharmacokinetics / pharmacodynamics
·Incidence of major adverse effects
·Decide whether it is ethical to continue testing in humans
Methods
·Relatively small number of participants
·Participants often not true target population
·Sometimes dose escalation
·Sometimes no comparison group