February, 2003
© 2000, 2001, 2003 Scott S. Emerson, M.D., Ph.D.
Screening Studies: 11
Preliminary Studies in Screening
Scenario 2: Use of pilot studies (cont.)
1,000,000 subjects available for clinical trials
·625,000 subjects in pilot studies of 12,500 new treatments
·374,500 subjects in confirmatory trials of 749 new treatments